'Keep them well': New cystic fibrosis medications move closer to a cure

[inanna]

By Amina Zafar, CBC News
Posted: Aug 07, 2017 5:00 AM ET

...

Results of a new drug trial published in The Lancet Respiratory Medicine journal suggest the next generation of medications, known as CFTR modulators, show potential to actually correct the genetic defect that causes cystic fibrosis and halt the disease's destructive progression.

<snip>

Currently, cystic fibrosis is managed mainly with antibiotics and mucolytics, which help patients to clear the mucus from their lungs before they become infected.

But CFTR modulators are designed to target the source of the problem rather than simply control the symptoms.

By intervening earlier with the new medications, researchers are hopeful children with the disease will be able to avoid the kind of accumulation of scarring and other damage experienced by people like Gagnon.

...

http://www.cbc.ca/news/health/cystic-fibrosis-1.4229844

[Dustlawyer]

1. Great news, though way too late for my son Joshua.

He was the case that doctors learned that you cannot give too many digestive engines or they will eat through you intestines.

[sharp_stick]

2. I'm sorry

CF has taken many people far too early. Research has been incredibly difficult and slow to get results.

I hope this is the beginning of new treatments because we've hit the wall with the older ones.

[inanna]

3. Saddened to hear this.

CF is a terrible disease, but let's hope we are making some progress.